ABERRANT POST-TRANSLATIONAL MODIFICATIONS (PTMS) IN METHYL- AND PROPIONIC ACIDEMIA AND A MUTANT SIRTUIN (SIRT) TO METABOLIZE PTMS
Patent Cooperation Treaty
PCT/US2021/028228
Filed on 2021-04-20
PCT/US2021/028228
Filed on 2021-04-20
Targeted Integration Into The Albumin (Alb) Locus As A Treatment For Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MUT) Deficiency
US Application 17/267,482
Filed on 2021-02-09
Filed on 2021-02-09
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
Mexico
MX/a/2021/001062
Filed on 2018-10-30
MX/a/2021/001062
Filed on 2018-10-30
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
Australia
2018436152
Filed on 2018-10-30
2018436152
Filed on 2018-10-30
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
Mexico
MX/A/2021/000638
Filed on 2019-07-16
MX/A/2021/000638
Filed on 2019-07-16
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
Brazil
BR112021000675-3
Filed on 2019-07-16
BR112021000675-3
Filed on 2019-07-16
NON-DISRUPTIVE GENE THERAPY FOR THE TREATMENT OF MMA
European Patent
18929532.2
Filed on 2018-10-30
18929532.2
Filed on 2018-10-30
METHODS AND COMPOSITIONS OF MMA CONSTRUCTS AND VECTORS
South Korea
10-2021-7004181
Filed on 2019-07-16
10-2021-7004181
Filed on 2019-07-16