OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
Australia
2023274161
Filed on 2023-11-30
2023274161
Filed on 2023-11-30
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
Singapore
10202303471P
Filed on 2023-12-11
10202303471P
Filed on 2023-12-11
HIGH CONCENTRATION METHYLCOBALAMIN OR COMBINATION OF METHYL- AND HYDROXOCOBALAMIN FOR THE TREATMENT OF COBALAMIN C DEFICIENCY DISORDERS
US Application 18/032,132
Filed on 2023-04-14
Filed on 2023-04-14
NOVEL ADENO-ASSOCIATED VIRAL (AAV) VECTORS TO TREAT HEREDITARY METHYLMALONIC ACIDEMIA (MMA) CAUSED BY METHYLMALONYL-COA MUTASE
(MMUT) DEFICIENCY
US Application 18/026,421
Filed on 2023-03-15
Filed on 2023-03-15
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
Macao
J/6735
Filed on 2022-12-23
J/6735
Filed on 2022-12-23
GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE ALPHA
Patent Cooperation Treaty
PCT/US2022/082527
Filed on 2022-12-29
PCT/US2022/082527
Filed on 2022-12-29
GENE THERAPY FOR COMBINED METHYLMALONIC ACIDEMIA/ACIDURIA AND HYPERHOMOCYSTEINEMIA/HOMOCYSTINURIA, COBALAMIN C TYPE, AND DEFICIENCY OF MMACHC
US Application 18/056,356
Filed on 2022-11-17
Filed on 2022-11-17
ABERRANT POST-TRANSLATIONAL MODIFICATIONS(PTMS) IN METHYL- AND PROPIONIC ACIDEMIA AND A MUTANT SIRTUIN (SIRT) TO METABOLIZE PTMS
US Application 17/923,394
Filed on 2022-11-04
Filed on 2022-11-04
SYNTHETIC GENES FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE BETA
US Application 17/766,067
Filed on 2022-04-01
Filed on 2022-04-01