A Method of Detecting Molecules in Proximity to a Target Molecule in a Sample Read more about A Method of Detecting Molecules in Proximity to a Target Molecule in a Sample US Application 62/211,160Filed on 2015-08-28
Tagged Form Of Mut Enzyme, Genetic Constructs Incorporating It, And Its Use In Gene Therapy Read more about Tagged Form Of Mut Enzyme, Genetic Constructs Incorporating It, And Its Use In Gene Therapy US Application 62/152,520Filed on 2015-04-24
Sialylation-increasing Therapies For Diseases Associated With Oxidative Stress Read more about Sialylation-increasing Therapies For Diseases Associated With Oxidative Stress US Application 62/120,742Filed on 2015-02-25
VIRAL GENE THERAPY AS TREATMENT FOR CHOLESTEROL STORAGE DISEASE OR DISORDER Read more about VIRAL GENE THERAPY AS TREATMENT FOR CHOLESTEROL STORAGE DISEASE OR DISORDER US Application 62/144,702Filed on 2015-04-08
METHODS OF TREATING PXE WITH TNAP INHIBITORS Read more about METHODS OF TREATING PXE WITH TNAP INHIBITORS US Application 62/058,505Filed on 2014-10-01
Compounds and Method for Treating PARP1-Deficient Cancers Read more about Compounds and Method for Treating PARP1-Deficient Cancers US Application 61/988,502Filed on 2014-05-05
Compounds and Method for Treating PARP1-Deficient Cancers Read more about Compounds and Method for Treating PARP1-Deficient Cancers US Application 61/930,291Filed on 2014-01-22
METHODS FOR TREATING LEUKEMIA AND DISORDERS MEDIATED BY MLL FUSION PROTEINS Read more about METHODS FOR TREATING LEUKEMIA AND DISORDERS MEDIATED BY MLL FUSION PROTEINS US Application 61/736,459Filed on 2012-12-12
Compositions and Methods for Predicting Age of Onset of A Lysosomal Storage Disease or a Disease Associated with a Lysosomal Defect Read more about Compositions and Methods for Predicting Age of Onset of A Lysosomal Storage Disease or a Disease Associated with a Lysosomal Defect US Application 61/781,807Filed on 2013-03-14
Biomarker For Hyposialylation Disorders Read more about Biomarker For Hyposialylation Disorders US Application 61/785,094Filed on 2013-03-14