CODON-OPTIMIZED HUMAN NPC1 GENES FOR THE TREATMENT OF NIEMANN-PICK TYPE C1 DEFICIENCY AND RELATED CONDITIONS
Technology
E-100-2017
Patent ID
E-100-2017-0-PCT-02
Country
PCT
Application Type
PCT
Patent Status
Expired
Patent Number
Publication Number
Application Number
PCT/US2018/038584
IC
NHGRI
Date Filed
Date Issued
Patent PDF