Targeted Integration Into The Albumin (Alb) Locus As A Treatment For Hereditary Methylmalonic Acidemia (MMA) Caused By Methylmalonyl-coA Mutase (MUT) Deficiency

Technology
E-034-2019
Patent ID
E-034-2019-0-PCT-02
Country
PCT
Application Type
PCT
Patent Status
Expired
Patent Number
 
Publication Number
WO 2020/032986
Application Number
PCT/US2018/058307
IC
NHGRI
Date Filed
Date Issued
 
Patent PDF