Targeting The 5'UTR Of Survival Motor Neuron 2 (SMN2) To Increase Its Expression In A Disease Model Of Spinal Muscular Atrophy (SMA)

Technology
E-208-2020
Patent ID
E-208-2020-0-US-01
Country
US
Application Type
 
Patent Status
Abandoned
Patent Number
 
Publication Number
 
Application Number
62/796,748
IC
NINDS
Date Filed
Date Issued
 
Patent PDF
 
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TAB-3720     Targeting the 5’UTR of Survival Motor Neuron 2 (SMN2) with Antisense Oligonucleotides to Increase Expression for the Treatment of Spinal Muscular Atrophy