GENE THERAPY CONSTRUCTS FOR THE TREATMENT OF PROPIONIC ACIDEMIA CAUSED BY MUTATIONS IN PROPIONYL-COA CARBOXYLASE ALPHA

Technology
E-034-2022
Patent ID
E-034-2022-0-PCT-02
Country
PCT
Application Type
PCT
Patent Status
Pending
Patent Number
 
Publication Number
WO 2023/130003
Application Number
PCT/US2022/082527
IC
NHGRI
Date Filed
Date Issued
 
Patent PDF