CODON-OPTIMIZED HUMAN NPC1 GENES FOR THE TREATMENT OF NIEMANN-PICK TYPE C1 DEFICIENCY AND RELATED CONDITIONS

Technology
E-100-2017
Patent ID
E-100-2017-0-US-05
Country
US
Application Type
National Stage
Patent Status
Pending
Patent Number
 
Publication Number
US-2017-0067042
Application Number
16/623,863
IC
NHGRI
Date Filed
Date Issued
 
Patent PDF